Abstract

Gene Therapy: An Overview

Shivani Kachroo and Sivakumar JT Gowder

The idea of gene therapy is unique; it works by the addition of a healthy gene in place of a defective or faulty candidate genes so that the changes in the gene function in the patient’s body are retained and restored. It represents a means to treat a disease in a more innovative way by use of genetic materials leading to expression of proteins in the cells which interfere with the synthesis of proteins to treat diseases. Different vector systems perform gene transfer with certain advantages and disadvantages.