Disease-specific Induced Pluripotent Stem Cell Modeling: Insights into the Pathophysiology of Valosin Containing Protein (VCP) Disease

Eric Dec^1,2#, David Ferguson^1,2#, Angèle Nalbandian^1,2#, Matthew Gargus¹, Veeral Katheria¹, Abel Ibrahim¹, Maya Hatch¹, Prachi Rana², Mary Lan¹, Katrina J Llewellyn¹, Hans Keirstead² and Virginia E Kimonis^1,2*

¹Division of Genetics and Metabolism, Department of Pediatrics, University of California-Irvine, Irvine, CA 92697, USA

²Anatomy and Neurobiology, Reese-Irvine Research Center, Sue and Bill Gross Stem Cell Research Center, University of California-Irvine, Irvine, CA 92697, USA

^#Contributed equally to this work